Gene Therapy Gets Fda Approval -- And A $2 Million Price Tag

The US Food and Drug Administration approved a treatment Friday for a genetic disease called spinal muscular atrophy that causes infants' muscles to waste away, potentially killing them before age 2.

Topics:  us food   drug administration   gene   
BING NEWS:
  • Ocugen: Two Gene Therapy Data Readouts In 2024 To Drive Value
    Ocugen is gearing up to report results from the two phase 1/2 studies for the treatment of patients with GA and Stargardt Disease. Check out why OCGN stock is a buy.
    04/19/2024 - 10:05 am | View Link
  • Philadelphia region's life sciences tech hub seeks $75M in federal funds
    A coalition of more than 100 organizations in the Philadelphia region has submitted a funding proposal to the government outlining its strategy for advancing the local life sciences industry.
    04/17/2024 - 4:41 am | View Link
  • Stanford doctors help develop first FDA-approved gene-editing treatment
    The FDA recently approved Casgevy, a gene-editing medical treatment which uses CRISPR/Cas9 technology to treat sickle cell disease. Casgevy, which two Stanford faculty members contributed to via drug ...
    04/8/2024 - 8:28 pm | View Link
  • Rocket Pharmaceuticals: Cautiously Optimistic (Rating Upgrade)
    Rocket Pharmaceuticals has potential FDA approvals for its gene therapies and pipeline includes promising therapies. Find out why RCKT stock remains a buy.
    04/5/2024 - 4:50 am | View Link
  • FDA approves gene therapy for metachromatic leukodystrophy, the tenth for a genetic disease and the priciest yet
    The US FDA has approved Orchard ... is the tenth gene augmentation therapy to secure approval in the US for a genetic disease. Priced at US$4.25 million, it is the world’s most expensive therapy ...
    03/27/2024 - 1:01 pm | View Link
  • More

 

Welcome to Wopular!

Welcome to Wopular

Wopular is an online newspaper rack, giving you a summary view of the top headlines from the top news sites.

Senh Duong (Founder)
Wopular, MWB, RottenTomatoes

Subscribe to Wopular's RSS Fan Wopular on Facebook Follow Wopular on Twitter Follow Wopular on Google Plus

MoviesWithButter : Our Sister Site

More Health News